Comments on Spinal Muscular Atrophy Research News: From skin cells to motor neurons

2013? Mogul Using $100 Million in Race to Cure Da...

2011-09-07T09:16:29.882-05:00

2013?

Mogul Using $100 Million in Race to Cure Daughter Lures Novartis

The malady makes the nerve cells that control muscles gradually deteriorate. There are no treatments, let alone a cure, Bloomberg Markets magazine reports in its October issue. Worse still, while the gene causing the ailment had recently been discovered, nobody in the drug industry was doing much about it, he says.

"I was fearful and anxious that treatments would be developed, but far too late to save Arya," says Singh, 42, who founded and runs New York hedge fund TPG-Axon Capital Management LP, which has $8.1 billion in assets. "We didn't want to find out 25 years later that the science was really there but there isn't a drug because nobody focused on it."

The foundation has pumped $13 million into PTC Therapeutics Inc. in South Plainfield, New Jersey, which has produced a pill that increases the life span of mice with SMA. It also has funded a scientist whose research has led to an injectable drug developed by Isis Pharmaceuticals Inc. of Carlsbad, California. That treatment may enter human trials before year's end. Singh says he'll enroll Arya if that drug gets to the testing phase before others.

Read more: http://www.sfgate.com/cgi-bin/article.cgi?f=/g/a/2011/09/06/bloomberg1376-LR3QQA07SXKZ01-0HM8202AR69TE4RI6U6L7SK5G4.DTL#ixzz1XHAXXZbJ

Jerry Lewis/MDA saga hardly symphonic as orchestra...

2011-09-04T10:21:58.573-05:00

Jerry Lewis/MDA saga hardly symphonic as orchestra for his final performance is called off

Lewis has most recently focused his philanthropic efforts on the Muscular Dystrophy Foundation Australia, which is not affiliated with the MDA.

http://www.lasvegassun.com/blogs/kats-report/2011/aug/31/jerry-lewismda-saga-hardly-symphonic-orchestra-his/

I have not seen one comment at any research/founda...

2011-09-02T11:37:26.526-05:00

I have not seen one comment at any research/foundation sites dealing what the impact for acceleration to cures will be from this advancement. I find that strange. Any one find anything?
please post.